Disease areas
Biotech companies by disease area
The companies we cover, grouped by the diseases their open catalysts and active programs target. A company working in several areas appears in each.
- Blood cancers32 companies · 20 upcoming catalystsLeukemia, lymphoma, myeloma and related cancers
- Lung cancer32 companies · 15 upcoming catalystsNon-small cell and small cell lung cancer and mesothelioma
- Breast and gynecologic cancers35 companies · 12 upcoming catalystsBreast, ovarian, endometrial and cervical cancer
- Gastrointestinal cancers39 companies · 16 upcoming catalystsColorectal, pancreatic, gastric, liver and biliary cancer
- Other cancers65 companies · 55 upcoming catalystsProstate, bladder, kidney, skin, brain, head and neck cancers, sarcomas and solid tumors in general
- Eye diseases22 companies · 27 upcoming catalystsRetinal disease, macular degeneration, uveitis and other eye conditions
- Kidney diseases25 companies · 11 upcoming catalystsIgA nephropathy, lupus nephritis, FSGS and other kidney conditions
- Neuromuscular diseases28 companies · 26 upcoming catalystsMuscular dystrophies, myasthenia gravis, myositis and related conditions
- Neurology and pain68 companies · 45 upcoming catalystsALS, Alzheimer's, Parkinson's, multiple sclerosis, epilepsy, pain and other nervous system conditions
- Psychiatric disorders21 companies · 11 upcoming catalystsDepression, schizophrenia, anxiety, PTSD, addiction and related conditions
- Blood disorders15 companies · 6 upcoming catalystsSickle cell disease, thalassemia, hemophilia, PNH and other non-cancer blood conditions
- Infectious diseases16 companies · 8 upcoming catalystsHepatitis B and D, COVID-19, influenza, RSV, bacterial infections and vaccines
- Lung and respiratory diseases24 companies · 7 upcoming catalystsPulmonary hypertension, pulmonary fibrosis, asthma, COPD and cystic fibrosis
- Liver and digestive diseases26 companies · 18 upcoming catalystsMASH, ulcerative colitis, Crohn's disease, cholestatic liver disease and other digestive conditions
- Obesity, diabetes and heart disease47 companies · 40 upcoming catalystsObesity, diabetes, high cholesterol, heart failure, cardiomyopathy and other heart conditions
- Skin diseases26 companies · 21 upcoming catalystsAtopic dermatitis, psoriasis, hidradenitis suppurativa, alopecia, wounds and other skin conditions
- Autoimmune and inflammatory diseases53 companies · 25 upcoming catalystsRheumatoid arthritis, lupus, Sjögren's disease, gout, transplant rejection and other immune conditions
- Endocrine and bone diseases15 companies · 10 upcoming catalystsThyroid, parathyroid, growth and pituitary disorders, menopause and bone diseases
- Rare genetic and metabolic diseases26 companies · 15 upcoming catalystsEnzyme deficiencies, lysosomal storage diseases, ATTR amyloidosis and other inherited conditions